| Targeted genome editing in human repopulating haematopoietic stem cells P Genovese, G Schiroli, G Escobar, T Di Tomaso, C Firrito, A Calabria, ... Nature 510 (7504), 235-240, 2014 | 687 | 2014 |
| Precise gene editing preserves hematopoietic stem cell function following transient p53-mediated DNA damage response G Schiroli, A Conti, S Ferrari, L Della Volpe, A Jacob, L Albano, S Beretta, ... Cell stem cell 24 (4), 551-565. e8, 2019 | 257 | 2019 |
| Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1 G Schiroli, S Ferrari, A Conway, A Jacob, V Capo, L Albano, T Plati, ... Science translational medicine 9 (411), eaan0820, 2017 | 209 | 2017 |
| Cyclosporine H overcomes innate immune restrictions to improve lentiviral transduction and gene editing in human hematopoietic stem cells C Petrillo, LG Thorne, G Unali, G Schiroli, AMS Giordano, F Piras, ... Cell Stem Cell 23 (6), 820-832. e9, 2018 | 100 | 2018 |
| NY-ESO-1 TCR single edited stem and central memory T cells to treat multiple myeloma without graft-versus-host disease S Mastaglio, P Genovese, Z Magnani, E Ruggiero, E Landoni, B Camisa, ... Blood, The Journal of the American Society of Hematology 130 (5), 606-618, 2017 | 74 | 2017 |
| Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patients B Diez, P Genovese, FJ Roman‐Rodriguez, L Alvarez, G Schiroli, ... EMBO molecular medicine 9 (11), 1574-1588, 2017 | 58 | 2017 |
| Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome V Vavassori, E Mercuri, GE Marcovecchio, MC Castiello, G Schiroli, ... EMBO Molecular Medicine 13 (3), e13545, 2021 | 36 | 2021 |
| Sleep exerts lasting effects on hematopoietic stem cell function and diversity CS McAlpine, MG Kiss, FM Zuraikat, D Cheek, G Schiroli, H Amatullah, ... Journal of Experimental Medicine 219 (11), e20220081, 2022 | 29 | 2022 |
| Retrieval of vector integration sites from cell-free DNA D Cesana, A Calabria, L Rudilosso, P Gallina, F Benedicenti, G Spinozzi, ... Nature Medicine 27 (8), 1458-1470, 2021 | 27 | 2021 |
| Therapeutic gene editing in CD34 (+) hematopoietic progenitors from Fanconi anemia patients. EMBO Mol Med 9: 1574–1588 B Diez, P Genovese, FJ Roman-Rodriguez, L Alvarez, G Schiroli, ... | 19 | 2017 |
| Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1. Sci Transl Med 2017; 9 G Schiroli, S Ferrari, A Conway, A Jacob, V Capo, L Albano | 6 | |
| 481. Targeted genome editing in Mouse hematopoietic stem/progenitor cells (HSPC) to model gene correction of SCID-X1 G Schiroli, P Genovese, MC Castiello, V Capo, PD Gregory, MC Holmes, ... Molecular Therapy 23, S191, 2015 | 5 | 2015 |
| Defocus Corrected Large Area Cryo-EM (DeCo-LACE) for label-free detection of molecules across entire cell sections J Elferich, G Schiroli, DT Scadden, N Grigorieff Elife 11, e80980, 2022 | 4 | 2022 |
| Efficient targeted integration in human t cells with crispr-cas9 for the treatment of x-linked hyper-igm syndrome CM Margulies, F Buquicchio, G Schiroli, V Vavassori, J Gori, K Gogi, ... Molecular Therapy 26 (5), 237-237, 2018 | 2 | 2018 |
| The bone marrow stroma in human myelodysplastic syndrome reveals alterations that regulate disease progression YS Kfoury, F Ji, E Jain, M Mazzola, G Schiroli, A Papazian, F Mercier, ... Blood Advances 7 (21), 6608-6623, 2023 | 1 | 2023 |
| Limited plasticity of monocyte fate and function associated with epigenetic scripting at the level of progenitors C Rhee, EW Scadden, LP Wong, G Schiroli, MC Mazzola, PL Chea, ... Blood 142 (7), 658-674, 2023 | 1 | 2023 |
| Liquid-Biopsy-Integration-Site-Sequencing Allows Safety Studies and Longitudinal Monitoring of Vector Integration Sites in LV and AAV-Based In-Vivo GT Applications D Cesana, A Calabria, L Rudilosso, P Gallina, F Benedicenti, G Spinozzi, ... MOLECULAR THERAPY 29 (4), 129-129, 2021 | 1 | 2021 |
| 42. Correction of SCID-X1 by targeted genome editing of hematopoietic stem/progenitor cells (HSPC) in the mouse model G Schiroli, P Genovese, V Capo, MC Castiello, L Albano, MC Holmes, ... Molecular Therapy 24, S18-S19, 2016 | 1 | 2016 |
| In Vivo Delivery of RNA By Lipid Nanoparticles (LNP) to Hematopoietic Stem Cells and T Cells in Humanized Mice and Non-Human Primates MT Monte, H Gu, L Saunders, M Gupta, L Liu, A Wangweerawong, ... Blood 142 (Supplement 1), 4818-4818, 2023 | | 2023 |
| Deploying an RNA-Based Gene Writer System and Lipid Nanoparticle (LNP) Delivery to Generate Functional Chimeric Antigen Receptor (CAR) T Cells with in Vitro and In Vivo Anti … MS Magee, A De Iaco, J Rodriguez, JB Rottman, D Liu, G Schiroli, ... Blood 142, 2073, 2023 | | 2023 |
